Beta thalassemia
Every day, people living with serious diseases strive to be more than their disease — to be defined by what they can dream and hope and achieve, not by what limits them. Our commitment to people with serious diseases is uncompromising and goes beyond our research and development (R&D) and medicines.
Working with the beta thalassemia community
We work with organizations that help people with transfusion-dependent beta thalassemia (TDT) live active, full lives.
We are committed to investigating and advancing approaches to treat the underlying cause of TDT. Vertex seeks to identify opportunities where we can support, empower, learn from and engage with the beta thalassemia community and ensure their voices are represented and incorporated into all that we do.
Looking at life differently: Living with beta thalassemia
Meet Gaia, Pranav and the Antonelli family as they share their experiences living with transfusion-dependent beta thalassemia (TDT), a serious and life-shortening blood disorder. Watch the videos below to learn more about what it’s like to live with TDT, from the daily impact of this disease to their perspectives on life.
Living with TDT
Gaia is a journalist from Italy, living with TDT. Find out how the management of TDT and its complications impacts every part of her life.
Embracing life with TDT
People living with TDT are more than their disease. Pranav doesn’t let his diagnosis define him; hear how he’s embracing life.
The time it takes away
For people living with TDT, time is marked by lifesaving blood transfusions. Traci and her three daughters share the burden of managing their TDT and the time it takes away from their daily lives.
Working with the beta thalassemia community
We work with organizations that help people with TDT live active, full lives.
We are committed to investigating and advancing approaches to treat the underlying cause of TDT. Vertex seeks to identify opportunities where we can support, empower, learn from and engage with the beta thalassemia community and ensure their voices are represented and incorporated into all that we do.
Vertexians with the thalassemia community in D.C. at the 2023 Cooley's Anemia Foundation Care Walk.
Supporting the beta thalassemia community
We are honored to support our beta thalassemia community partners to raise awareness and understanding of thalassemia, including Cooley’s Anemia Foundation, the Thalassemia International Federation and others.
Learn about our work in beta thalassemia
To learn more about our beta thalassemia studies in the U.S., visit our clinical trials website. For information about non-U.S. sites, visit clinicaltrials.gov.
Featured stories
Research and beyond: Our commitment to the beta thalassemia community
We’ve been working with the beta thalassemia community since the inception of our research program in 2015. Learn more about our efforts and commitments around the globe.
Give blood and keep the world beating: Voices of gratitude on World Blood Donor Day
On World Blood Donor Day, hear from two individuals living with sickle cell disease and transfusion-dependent beta thalassemia as they share their stories, shed light on their struggles, and emphasize the impact blood donation has had on their disease and quality of life.
Behind the smile, a look into the lives of people living with serious illness
Learn how we explore the daily lives of those living with debilitating disease to help inform our mission.
